| Delivery | Pipeline | POC | Pre-IND | IND | Phase Ⅰ | Phase Ⅱ/Ⅲ |
| β-thalassemia |
|
| Sickle cell disease |
|
| Hypertriglyceridemia/Familial chylomicronemia |
|
| ASCVD/Hyperlipoproteinemia |
|
| Homozygous Familial Hypercholesterolemia |
|
| Inherited metabolic disorder |
|
| Inherited metabolic disorder |
|
| Non-liver targeting |
|
